PTC Therapeutics, Inc. (NASDAQ: PTCT) shares nearly doubled this past Friday after the company received a positive opinion from the Committee for Medicinal Products for Human Use (CHMP) in Europe for translarna, which is the branded name given to ataluren, the company's lead investigational compound. According to a press release, following its request for a reexamination of translarna as a treatment for nonsense mutation Duchenne muscular dystrophy, the CHMP recommended the conditional marketing authorization of the compound. This recommendation will be taken into consideration by the European Medicines Agency on whether to grant EU market approval over the coming months.
PTC Therapeutics, Inc., a biopharmaceutical company, focuses on the discovery and development of orally administered, proprietary small-molecule drugs that target post-transcriptional control processes. Its lead product candidate is ataluren for the treatment of patients with genetic disorders that arise from a type of genetic mutation known as a nonsense mutations or nmCF.
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Prosensa Holding N.V. (NASDAQ: RNA) shares climbed higher this past Friday after the CHMP gave a positive opinion to Ataluren from PTC Therapeutics. Following the news, TheStreet's Adam Feuerstein stated on Twitter that Prosensa (RNA) "has to be a lock approval for exon 51 DMD in EU."
Prosensa Holding N.V., a biotechnology company, engages in the discovery and development of ribonucleic acid-modulating therapeutics for the treatment of genetic disorders. The company’s products focus on the treatment of neuromuscular and neurodegenerative disorders, including duchenne muscular dystrophy (DMD), myotonic dystrophy, and huntington’s diseases.
Get more information on Prosensa Holding N.V. and free access to the in depth equity report at” www.TrendingWallStreet.com/stockquote/RNA
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